Ultragenyx Pharmaceutical Inc.
NEWS
Collaboration is key to faster breakthroughs. The NIH, FDA, and 15 private organizations have announced they are joining forces for the sake of the 30 million Americans suffering from a rare disease.
It was yet another busy week for clinical trial news. Here’s a look.
Redosing is a large and growing concern for gene therapy developers and regulators.
Several biotech and biopharmaceutical companies have announced new wins with the U.S. Food and Drug Administration (FDA), with these wins ranging from Investigational New Drug (IND) application approvals for cancer treatment candidates to Fast Track Designations for investigational agents aimed toward opioid use disorder (OUD).
Biopharma and life sciences companies strengthen their leadership teams and boards with these Movers & Shakers.
Gene therapy is still very much cutting-edge with the potential to cure incurable genetic diseases. Here’s some recent news in the space.
The Rare Disease Company Coalition’s 10 founding members have brought 22 treatments to market and currently have more than 160 rare disease programs in the works.
Biopharma and life science companies from across the globe strengthen their leadership teams and boards with these Movers & Shakers.
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