News
Drug Development
FDA
Drug Delivery
Deals
Business
Policy
Cell and Gene Therapy
Weight Loss
Rare Disease
Cancer
Job Trends
Artificial Intelligence
NextGen: Top Start Ups to Watch
Podcasts
Reports
Webinars
Press Releases
All News & Releases
Insights
Jobs
Career Advice
Companies
Hotbeds
More
Best Places to Work
Employer Resources
Post Jobs
Talent Solutions
Advertise
Submit a Press Release
SUBSCRIBE
Menu
SUBSCRIBE
Show Search
News
Drug Development
FDA
Drug Delivery
Deals
Business
Policy
Cell and Gene Therapy
Weight Loss
Rare Disease
Cancer
Job Trends
Artificial Intelligence
NextGen: Top Start Ups to Watch
Podcasts
Reports
Webinars
Press Releases
All News & Releases
Insights
Jobs
Career Advice
Companies
Hotbeds
More
Best Places to Work
Employer Resources
Post Jobs
Talent Solutions
Advertise
Submit a Press Release
Search Query
Submit Search
Search Results
Submit
Looking for jobs?
Search jobs
Close
726,110 Results
Type
Article (51240)
Company Profile (522)
Press Release (674348)
Section
Business (211954)
Career Advice (2063)
Deals (36433)
Drug Delivery (104)
Drug Development (85701)
Employer Resources (169)
FDA (16826)
Job Trends (15343)
News (359368)
Policy (33969)
Tag
Academia (2770)
Alliances (51809)
Alzheimer's disease (1356)
Approvals (16741)
Artificial intelligence (157)
Bankruptcy (362)
Best Places to Work (12003)
Biotechnology (386)
Breast cancer (195)
Cancer (1394)
Cardiovascular disease (121)
Career advice (1722)
Cell therapy (299)
Clinical research (68080)
Collaboration (474)
Compensation (253)
COVID-19 (2721)
C-suite (117)
Data (1392)
Diabetes (174)
Diagnostics (6430)
Earnings (87150)
Employer resources (147)
Events (116048)
Executive appointments (375)
FDA (17471)
Funding (432)
Gene therapy (214)
GLP-1 (665)
Government (4596)
Healthcare (19473)
Infectious disease (2819)
Inflammatory bowel disease (125)
Interviews (322)
IPO (16831)
Job creations (3778)
Job search strategy (1468)
Layoffs (457)
Legal (8100)
Lung cancer (200)
Manufacturing (202)
Medical device (13598)
Medtech (13603)
Mergers & acquisitions (19723)
Metabolic disorders (476)
Neuroscience (1701)
NextGen Class of 2024 (6928)
Non-profit (4745)
Northern California (1671)
Obesity (275)
Opinion (207)
Patents (117)
People (58714)
Pharmaceutical (103)
Phase I (21219)
Phase II (29914)
Phase III (22319)
Pipeline (515)
Postmarket research (2814)
Preclinical (9221)
Radiopharmaceuticals (255)
Rare diseases (282)
Real estate (6135)
Regulatory (22755)
Research institute (2537)
Resumes & cover letters (357)
Southern California (1461)
Startups (3831)
United States (15431)
Vaccines (632)
Weight loss (206)
Date
Last 7 days (704)
Last 30 days (2458)
Last 365 days (36941)
2024 (36097)
2023 (41633)
2022 (52982)
2021 (57512)
2020 (55958)
2019 (48488)
2018 (36549)
2017 (33965)
2016 (33589)
2015 (39569)
2014 (33461)
2013 (28698)
2012 (30726)
2011 (31215)
2010 (29606)
Location
Africa (807)
Arizona (204)
Asia (40301)
Australia (6819)
California (3841)
Canada (1424)
China (300)
Colorado (174)
Connecticut (188)
Europe (89725)
Florida (527)
Georgia (132)
Illinois (398)
Indiana (223)
Maryland (641)
Massachusetts (3059)
Michigan (171)
Minnesota (299)
New Jersey (1099)
New York (1075)
North Carolina (830)
Northern California (1671)
Ohio (146)
Pennsylvania (917)
South America (1162)
Southern California (1461)
Texas (550)
Utah (108)
Washington State (412)
726,110 Results for "rare disease therapeutics inc".
Filters
Sort By
Relevance
Relevance
Newest
Oldest
Regulatory
FDA Action Alert: Applied Therapeutics Awaits Verdict on Rare Disease Therapy
With two decisions originally scheduled for this week already announced, including BridgeBio’s approval in ATTR-CM, the regulator has just one PDUFA on its plate this holiday week.
November 25, 2024
·
1 min read
·
Tristan Manalac
Rare diseases
Facing a Dearth of Big Pharma Interest, Rare Disease Players Get Creative to Fund R&D
A handful of billion-dollar deals in the rare disease space highlights the uptick in Big Pharma’s investment, but it’s still extremely low compared to the money flowing to more common indications.
November 20, 2024
·
7 min read
·
Heather McKenzie
Complete response letters
Applied Therapeutics Crashes After FDA Rejection of Rare Disease Drug
After extending its review period to evaluate additional submissions, the FDA ultimately denied Applied Therapeutics’ govorestat for galactosemia, citing “deficiencies” with the application. The biotech plans to meet with the regulator to discuss the best way forward for the drug.
December 2, 2024
·
3 min read
·
Tristan Manalac
Press Releases
ReviR Therapeutics and Kennedy’s Disease Association Partner to Advance Treatment for Rare Neuromuscular Disorder
November 26, 2024
·
3 min read
Press Releases
Unnatural Products Announces BridgeBio Exercises Option to License Macrocyclic Therapeutics for Development in Rare Diseases and Oncology
December 4, 2024
·
2 min read
Press Releases
Satellos to Participate in Oppenheimer Movers in Rare Disease Summit
December 3, 2024
·
1 min read
Press Releases
XORTX Announces Presentation at the Rare and Genetic Disease Summit
December 12, 2024
·
6 min read
Press Releases
Chemomab to Participate in Oppenheimer’s Movers in Rare Disease Summit
December 4, 2024
·
2 min read
Editorial
Sarepta, Biotech’s Regulatory Go-Getter, Signs Standout Rare Disease Deal
Not exactly known for its dealmaking, Sarepta Therapeutics has thrown down a massive wad of cash to work with Arrowhead Pharmaceuticals on RNAi-based medicines.
December 4, 2024
·
3 min read
·
Annalee Armstrong
Press Releases
HARMONY BIOSCIENCES TO PARTICIPATE IN OPPENHEIMER MOVERS IN RARE DISEASE SUMMIT
December 4, 2024
·
1 min read
1 of 72,611
Next
